FL
Overview
Gairdner Award
Biography
Gairdner Award. Associated with Bambino Gesù Hospital.
Affiliations & Institutions
Research Impact
5 Publications
0 Total Citations
Published In
N Engl J Med
Key Publications
CRISPR-Cas9 Gene Editing for Sickle Cell Disease and β-Thalassemia.
Exagamglogene Autotemcel for Severe Sickle Cell Disease.
Ruxolitinib for Glucocorticoid-Refractory Chronic Graft-versus-Host Disease.
Exagamglogene Autotemcel for Transfusion-Dependent β-Thalassemia.
Emapalumab in Children with Primary Hemophagocytic Lymphohistiocytosis.
Areas of Expertise
Medical Specialties
Clinical Knowledge & Procedures
Related Specialists
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